Synthetic Nucleic Acid Therapeutics: Basic Science, Delivery, and Drug Development (V6)
January 1-5, 2028
| Location to be Determined
David R. Corey, Punit P. Seth and Annemieke Aartsma-Rus
Saturday, January 1, 2028
| 4:00–8:00 PM |
Registration |
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| 6:00–8:00 PM |
Welcome Mixer |
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| 12:25–5:00 PM |
On Own for Lunch |
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| 8:00–8:10 AM |
Welcome Remarks (Joint) |
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| 8:10–9:00 AM |
Keynote Address (Joint) |
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| |
David R. Liu †, Broad Institute, HHMI, and Harvard University
Advances in Programmable Genome Editing Technologies |
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| 9:00–11:15 AM |
Technological Frontiers of Precision Genome Engineering (Joint) |
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| |
Prashant Mali †, University of California, San Diego
Genome and Cell Engineering with Circular RNAs |
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James Dahlman †, Georgia Tech / Emory Medical School
Targeted in vivo Genome Engineering with Designer Nanoparticles |
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Kristy Wood †, Intellia Therapeutics, Inc.
Development of in vivo CRISPR Medicines |
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| |
Short Talk(s) Chosen from Abstracts
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|
| 9:30–9:50 AM |
Coffee Break |
|
| 11:15–1:00 PM |
Poster Setup |
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| 11:25–12:25 PM |
Meet-the-Editor |
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| 1:00–10:00 PM |
Poster Viewing |
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| 2:30–4:30 PM |
Symposia Spotlight 1 |
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| |
Short Talks Chosen from Abstracts
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|
| 4:30–5:00 PM |
Coffee Available |
|
| 5:00–7:00 PM |
Delivery of Nucleic Acids |
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Daniel J. Siegwart †, University of Texas Southwestern Medical Center
Nanoparticle-Mediated Delivery |
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Julia Alterman †, UMass Chan Medical School
Novel Delivery Designs |
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| |
Flávia Sousa †, University of Groningen
Biodegradable Polymers |
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| |
Short Talk(s) Chosen from Abstracts
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|
| 7:00–8:00 PM |
Social Hour with Dinner |
|
| 8:00–11:00 AM |
Clinical Frontiers of Precision Genome Engineering (Joint) |
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| |
Benjamin P Kleinstiver †, Massachusetts General Hospital
Development of N=1 Clinical Trials |
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| |
Amy R. Simon †, Beam Therapeutics
Base Editing Clinical Trial |
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| |
Bill Lundberg †, CRISPR Therapeutics
Ex vivo/in vivo CRISPR-based Therapeutics |
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| |
Laura Sepp-Lorenzino †, Intellia Therapeutics
Perspectives on the Future of Genome Editing |
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| |
Short Talk(s) Chosen from Abstracts
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|
| 9:00–9:20 AM |
Coffee Break |
|
| 11:00–1:00 PM |
Poster Setup |
|
| 11:00–5:00 PM |
On Own for Lunch |
|
| 1:00–10:00 PM |
Poster Viewing |
|
| 3:00–4:30 PM |
Career Roundtable |
|
| 4:30–5:00 PM |
Coffee Available |
|
| 5:00–7:00 PM |
Rare Disease |
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| |
Annemieke Aartsma-Rus, Leiden University Medical Center
ASOs for Rare Disease |
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| |
David R. Corey, University of Texas Southwestern Medical Center
Gene Activation for Rare Disease |
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| |
Isabel Aznarez †, Stoke Therapeutics, Inc.
Gene Activation for Rare Disease |
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| |
Short Talk(s) Chosen from Abstracts
|
|
| 7:00–8:00 PM |
Social Hour with Dinner |
|
| 8:00–11:00 AM |
Preclinical/Clinical 1 |
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| |
Hien T Zhao †, Ionis Pharmaceuticals, Inc.
Ionis Update |
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| |
Brenda L. Bass †, University of Utah
RNA Editing |
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Alejandro Garanto †, Radboud University Medical Center
RNA Editing |
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| |
Adrian R. Krainer †, Cold Spring Harbor Laboratory
Talk Title to be Announced |
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| |
Short Talk(s) Chosen from Abstracts
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|
| 9:00–9:20 AM |
Coffee Break |
|
| 11:10–12:10 PM |
Patient/Family Roundtable |
|
| 12:10–5:00 PM |
On Own for Lunch |
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| 2:30–4:30 PM |
Symposia Spotlight 2 |
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| |
Short Talks Chosen from Abstracts
|
|
| 4:30–5:00 PM |
Coffee Available |
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| 5:00–6:15 PM |
Closing Session (Joint) |
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Punit P. Seth, Alnylam Pharmaceuticals
Alnylam Update |
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| |
Gerald Schwank †, University Zurich
Prime Editing for Inherited Metabolic Diseases |
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| |
Waseem Qasim †, University in London
Genome-Edited T Cell Therapies for Blood Cancer |
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Short Talk(s) Chosen from Abstracts
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|
| 6:15–7:00 PM |
Closing Keynote Address (Joint) |
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| |
John M. Maraganore †, City Therapeutics
Novel RNAi |
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| 7:00–7:15 PM |
Meeting Wrap-Up: Outcomes and Future Directions |
|
| 7:00–8:00 PM |
Social Hour with Dinner |
|
| 8:00–11:00 PM |
Entertainment |
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Wednesday, January 5, 2028
